How can CRISPR be used to treat human diseases?
Using the CRISPR system, researchers can precisely edit any target DNA locus - a feat that was not achievable using other gene editing tools. The possibility to edit a disease mutation to correct genetic errors creates opportunities for treating conditions that have long eluded the medical research community.
What is an example of an application of CRISPR technology for human health?
For example, CRISPR-based strategies could reduce infectious disease morbidity by gene editing mosquitoes to prevent transmission of malaria.
What does CRISPR do to diseases?
The CRISPR clinical trial aims to deactivate a mutated gene that causes liver cells to churn out misfolded forms of a protein called transthyretin (TTR), which build up on nerves and the heart and lead to pain, numbness, and heart disease.